Visit Speaker and Poster Presentations at the ASCGT; April 29- May 2, 2019 in Washington DC | ASC

Applied StemCell’s Therapeutic Development team will be at the American Society for Gene and Cell Therapy (ASCGT) to showcase research data from advances in genome editing in mouse and cell line models for treatment of monogenic disorders. Visit our speaker and poster presentations, and to discuss with our esteemed executives and scientists about our genome editing and gene editing platforms.

Event Details:

Date: April 29 – May 2

Venue: Washington Hilton, 1919 Connecticut Ave., NW, Washington, District of Columbia, 20009 USA

Meeting Agenda: https://annualmeeting.asgct.org/am19


 

PRESENTATION DETAILS:

Speaker Presentation Title: Hemophilia A Cured in Mice by CRISPR-based In Vivo Genome Editing of Human Factor FVIII

Author: Ruby Yanru Chen-Tsai, Hainan Chen, Avital Gilam, Zoya Gluzman-Poltorak, Ruhong Jiang, Ling-Jie Kong.

 


Poster #1 Title: Site-specific Genome Editing by CRISPR/Cas9 for Hemophilia A in Human and Non-Human Primate Cells

Author: Avital Gilam, Yin Zhang, Milena Veselinovic, Aanal Bhatt, Chengtao Yang, Tanushree Jaitly, Xinhao Wang, Hainan Chen, Mi Shi, Ivka Afrikanova, Ruhong Jiang, Ling-Jie Kong, Ruby Yanru Chen-Tsai, Zoya Gluzman-Poltorak.

 

Poster #2 Title: Adeno-associated Virus Serotypes Screening in Non-human Primates for Hemophilia A Genome Editing Treatment

Author: Zoya Gluzman-Poltorak, Avital Gilam, Yin Zhang, Ivka Afrikanova, Hainan Chen, Mi Shi, Milena Veselinovic, Aanal Bhatt, Alex Lyubimov, Matt Lindeblad, Yongmei Luo Chen, Todd Haryu, Ruhong Jiang, Ling-Jie Kong, Ruby Yanru Chen-Tsai.

 

 

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